NPS — IND process tracker

4 open chemical decisions

Lys position
Lys11HomoLysHomoHomoLysOrnithineLys12
v40.22 (Lys11) vs v40.9 (HomoLys11) head-to-head; v40.24 / v40.25 extra reach reads
Chain length
C16C18 satC18:1C20
C16 over-covered. v40.4 reads C18:1. C20 + saturated C18 are KAN gap-fills.
Truncation
1-201-131-12
Covered on both Nle11 (v40.2 / v40.3) and HomoLys11 (v40.10 / v40.11) scaffolds.
no linked tickets
C-terminus
-NH2-OH (free acid)
Only -NH2 in current queue. -OH gap-fill filed.

IND stages at a glance

StageOpenOverdueDoneNext due
Lead optimization 12002026-07-06
Stability + degradation2002026-08-14
PK (methods · studies · scaling/HED · PK-PD)23102026-06-26
Safety + immunogenicity4002026-07-21
GLP / CMC outsourcing8002026-09-08
Regulatory (AU CTN)3002026-09-15

Active studies (preclin.study, last 30 days)

STU-olden-dl-dmuo-st0067 · executing
NPSv40.9 1000ug vs. NPSv40.9 500ug vs. NPSv40.9 200ug vs. NPSv40.9 100ug vs. Placebo, subq, 100ul, 0.9% saline, n = 15
owner: — · updated 2026-06-24 18:48:01.219420+00:00
STU-26-NPS-20260629-003 · locked · KAN-89
Accelerated LC-MS stability triage for NPS lead-lock pair
Identify rapid parent loss or route-relevant degradation liabilities in the top NPS lead-lock candidates before the 2026-07-06 decision.
owner: iris · updated 2026-06-30 02:53:17.085537+00:00
STU-26-NPS-20260629-002 · locked · KAN-88
Human albumin functional-shift screen for lipidated NPS leaders
Test whether top lipidated NPS candidates preserve functional NPSR1 agonism in human albumin conditions relevant to human half-life translation.
owner: iris · updated 2026-06-30 02:23:56.962000+00:00
STU-26-NPS-20260629-001 · locked · KAN-87
Lead-lock same-plate IP1 for NPSR1 107I and 107N coverage
Determine whether the apparent 107I lead candidates retain potent full agonism on both hNPSR1 107I and 107N under matched IP1 conditions.
owner: iris · updated 2026-06-30 02:22:18.429192+00:00

Overdue across all stages (4)

KeyStatusDueAssigneeVendorCRO progressSummary
KAN-20Idea2026-06-22Moaraj Hasanno vendorpick vendor (-8d to due)SPPS synthesis - NPS 40.9
KAN-24Idea2026-06-26Moaraj Hasanno vendorpick vendor (-4d to due)PK study design + AEC (Animal Ethics Committee) protocol (mouse single-dose IV/SC)
KAN-21Idea2026-06-26Moaraj Hasanno vendorpick vendor (-4d to due)RP-HPLC purification + lyophilization (NXN + NPS)
KAN-16Idea2026-06-26Moaraj Hasanno vendorpick vendor (-4d to due)Peptide Synthesis & Purification

Compound × complete-assay coverage

"Complete" assay set: 107I IP1 · 107N IP1 · 107I FLIPR · 107N FLIPR · bArr · cAMP — same-plate, same-producer-batch. Cells show best EC50 in nM and run count. Empty cells (—) are missing reads.
CompoundQtySynthIn-vitro (cell assays)In-vivo + stability
IP1 (107I)IP1 (107N)FLIPR (107I)FLIPR (107N)bArr (107N)cAMP (107N)SC actigraphyEEGPK plasmaPK CSF/brainStability (LC-MS)
NPSv40.9
ANCHOR · Lead candidate — HomoLys11, 1-20, -NH2 — in all three head-to-heads
SF(Nω-methyl-Arg)N(Sar)VGTG(N-Me-Nle)(HomoLys)-K[(γ-E)-(C16 Pal)]-TSFQRAKS-NH2
not trackedmice reached0.00 nM · n=40.03 nM · n=60.62 nM · n=10.17 nM · n=11.47 nM · n=10.12 nM · n=10-6h: -33% sleep (NPSv41.18 500ug)
0-24h: -28% sleep (NPSv41.18 500ug)
DL-HGA4-st0078 · 12 Olden runs · latest 2026-06-29
post-lockpost-lockpost-lockplanned
NPSv40.22
Lys position · Lys11
SF(Nomega-methyl-Arg)N(Sar)VGTG(N-Me-Nle)K-K[(gamma-E)-(C16 Pal)]-TSFQRAKS-NH2
queued for SPPS0.07 nM · n=20.21 nM · n=2plannedpost-lockpost-lockpost-lockplanned
NPSv40.24
Lys position · HomoHomoLys11 (secondary — extra reach)
SF(Nomega-methyl-Arg)N(Sar)VGTG(N-Me-Nle)(HomoHomoLys)-K[(gamma-E)-(C16 Pal)]-TS…
not trackedqueued for SPPS0.10 nM · n=20.25 nM · n=4plannedpost-lockpost-lockpost-lockplanned
NPSv40.25
Lys position · Ornithine11 (secondary)
SF(Nomega-methyl-Arg)N(Sar)VGTG(N-Me-Nle)(Orn)-K[(gamma-E)-(C16 Pal)]-TSFQRAKS-N…
not trackedthrough HPLC0.27 nM · n=30.16 nM · n=4plannedpost-lockpost-lockpost-lockplanned
NPSv40.10
Truncation · 1-13 (hypothesis: default 1-20 wins; verify)
SF(Nω-methyl-Arg)N(Sar)VGTG(N-Me-Nle)(HomoLys)-K[(γ-E)-(C16 Pal)]-T-NH2
not trackedpartial0.11 nM · n=40.23 nM · n=10-6h: +22% sleep (EEG NPSv40.10 100ug)
0-24h: +71% sleep (EEG NPSv40.10 100ug)
DL-arPA-st0046 · 2 Olden runs · latest 2026-06-01
NPSv40.11
Truncation · 1-12 (hypothesis: default 1-20 wins; verify)
SF(Nω-methyl-Arg)N(Sar)VGTG(N-Me-Nle)(HomoLys)-K[(γ-E)-(C16 Pal)]-NH2
not trackedpartial0.09 nM · n=40.30 nM · n=1planned
NPSv41.1
C-terminus · -OH variant of v40.9 — critical for in-vivo effect-life decision
SF(Nomega-methyl-Arg)N(Sar)VGTG(N-Me-Nle)(HomoLys)-K[(gamma-E)-(C16 Pal)]-TSFQRA…
not trackedpartial0.17 nM · n=30-6h: -33% sleep (NPSv41.18 500ug)
0-24h: -28% sleep (NPSv41.18 500ug)
DL-HGA4-st0078 · 2 Olden runs · latest 2026-06-29
post-lockpost-lockpost-lock
NPSv40.23
Secondary · Nω,Nω-dimethyl-Arg3 — add to cell assays where we have it (lower priority)
SF(Nomega,Nomega-dimethyl-Arg)N(Sar)VGTG(N-Me-Nle)(HomoLys)-K[(gamma-E)-(C16 Pal…
not trackedqueued for SPPS0.13 nM · n=30.55 nM · n=3

Planned SC mouse studies (@Jigisha)

StudyArmsStatus / note
Lys11 SC studyNPSv40.9 · NPSv40.22 · NPSv40.24 · NPSv40.25@Jigisha — n≥20/group, 1-page plan, verify material first
Truncation SC studyNPSv40.9 · NPSv40.10 · NPSv40.11@Jigisha — n≥20/group, 1-page plan, verify material first
C-terminus SC studyNPSv40.9 · NPSv41.1@Jigisha — critical for finalising -NH2 vs -OH on in-vivo effect-life

Synthesis workstream (@Nico, @Hillary)

Chemistry ask (@Nico): one clean ≥95% pure in-house batch each of v40.9, v40.22, v40.24, v40.25, v41.1.
KeyStatusDueAssigneeVendorCRO progressSummary
KAN-20Idea2026-06-22Moaraj Hasanno vendorpick vendor (-8d to due)SPPS synthesis - NPS 40.9
KAN-21Idea2026-06-26Moaraj Hasanno vendorpick vendor (-4d to due)RP-HPLC purification + lyophilization (NXN + NPS)
KAN-16Idea2026-06-26Moaraj Hasanno vendorpick vendor (-4d to due)Peptide Synthesis & Purification

Analytical QC workstream (@Mo)

KeyStatusDueAssigneeVendorCRO progressSummary
KAN-17Idea2026-07-03Moaraj Hasanno vendorpick vendor (3d to due)Analytical QC / Mass Spec ID
KAN-14Idea2026-07-03Moaraj Hasanno vendorpick vendor (3d to due)Intact mass + full sequence confirmation MS/MS

In-vitro potency workstream (@Stephen)

KeyStatusDueAssigneeVendorCRO progressSummary
KAN-23Idea2026-07-17Moaraj Hasanno vendorpick vendor (17d to due)NPSR1 IP1 EC50 assay — NPS 40.9
KAN-18Idea2026-07-17Moaraj Hasanno vendorpick vendor (17d to due)In-vitro Potency (OX2 IP1 / EC50)

Mechanism + efficacy workstream (in-vitro target engagement, selectivity panel)

KeyStatusDueAssigneeVendorCRO progressSummary
KAN-40Idea2026-07-15Moaraj Hasanno vendorpick vendor (15d to due)In-vitro target engagement + selectivity panel
KAN-41Idea2026-08-05Moaraj Hasanno vendorpick vendor (36d to due)In-vivo efficacy / target-engagement model (mouse)
KAN-42Idea2026-08-31Moaraj Hasanno vendorpick vendor (62d to due)Mechanism-of-action omics readout + brain exposure
KAN-6Idea2026-08-31Moaraj Hasanno vendorpick vendor (62d to due)Efficacy & Mechanism (cells, mouse, omics)

Filed Iris gap-fills (review needed)

Some of these are now redundant with the 2026-06-30 state-of-the-union — see notes.
KANAxisStatus / note
KAN-90Chain lengthC20 lipid analog — DEFER: chain length is not a lead-lock decision per 2026-06-30 SoU (future-NPS lever)
KAN-91C-terminusFree-acid (-OH) analog — already in flight as NPSv41.1; close as duplicate
KAN-92Chain lengthSaturated C18 analog — DEFER (future-NPS lever)
KAN-93CMCCMC + accelerated-degradation — re-scope as external-contractor work (Helena owns)

Active engagements (3)

Populated from preclin.cro_capability — writes flow from forwarded CRO emails + Slack @iris cro.
VendorWorkstreamStatusOwnerCRO progressLast engagementNotes
Charles River Laboratoriesglp_tox_rodentno contractmelissano_contract2026-06-30 📧CRL BD contact Hank Arrington reached out to initiate CDA or MSA. Moaraj confirm
iHisto Inc.histologyPOmelissaPO live · Safety tissues shipped to iHisto Inc. (Salem, MA) 2026-06-30 📧Safety tissues shipped to iHisto Inc. (Salem, MA) via UPS Next Day Air Early on
Charles River Laboratoriessafety_pharm_ich_s7ano contractmelissano_contract2026-06-30 📧CRL engaged to scope full nonclinical package including safety pharmacology as p

Open gaps (17) — KAN tickets with no contracted vendor

KANDueAssigneeSummary
KAN-402026-07-15Moaraj HasanIn-vitro target engagement + selectivity panel
KAN-432026-07-21Moaraj HasanIn-vitro safety pharmacology (hERG, cardiovascular liability)
KAN-412026-08-05Moaraj HasanIn-vivo efficacy / target-engagement model (mouse)
KAN-442026-08-10Moaraj HasanImmunogenicity / ADA assay strategy + in-silico risk
KAN-452026-08-31Moaraj HasanGLP tox study design + DART deferral justification
KAN-422026-08-31Moaraj HasanMechanism-of-action omics readout + brain exposure
KAN-72026-08-31Moaraj HasanSafety & Immunogenicity (DART defer, ADA)
KAN-62026-08-31Moaraj HasanEfficacy & Mechanism (cells, mouse, omics)
KAN-712026-09-08Moaraj HasanGMP clinical batch manufacture (API) + batch record + CoA
KAN-752026-09-15Moaraj HasanClinical protocol + synopsis (FIH SAD)
KAN-692026-09-15Moaraj HasanGenotoxicity battery (Ames + in vitro micronucleus)
KAN-742026-09-22Moaraj HasanAuthor Investigator's Brochure (IB)
KAN-722026-09-22Moaraj HasanDrug product CMC: sterile injectable formulation, fill-finish, container-closure
KAN-682026-09-22Moaraj HasanGLP repeat-dose toxicology study (non-rodent) - execution + report
KAN-732026-09-29Moaraj HasanICH Q1A stability program on clinical API + DP lots
KAN-92026-09-30Moaraj HasanAU CTN Regulatory Package & Submission
KAN-82026-09-30Moaraj HasanGLP Outsourcing & CMC (engage on clinical lead)

Stability + degradation

2 open 0 done
KeyStatusDueAssigneeVendorCRO progressSummary
KAN-15Idea2026-08-14Moaraj Hasanno vendorpick vendor (45d to due)Forced degradation study + impurity criteria
KAN-2Idea2026-08-14Moaraj Hasanno vendorpick vendor (45d to due)Degradation & Stability (HF-X Orbitrap)

PK (methods · studies · scaling/HED · PK-PD)

23 open 1 overdue 0 done
CRO progress (Drive): 📁 Preclinical development
KeyStatusDueAssigneeVendorCRO progressSummary
KAN-24Idea2026-06-26Moaraj Hasanno vendorpick vendor (-4d to due)PK study design + AEC (Animal Ethics Committee) protocol (mouse single-dose IV/SC)
KAN-29Idea2026-06-30Moaraj Hasanno vendorpick vendor (0d to due)Reference standards, IS qualification + stock/working solutions
KAN-25Idea2026-06-30Moaraj Hasanno vendorpick vendor (0d to due)Dose formulation, dose verification, and vehicle bridging
KAN-30Idea2026-07-08Moaraj Hasanno vendorpick vendor (8d to due)Calibration curve + selectivity/specificity (ICH M10)
KAN-11Idea2026-07-10Moaraj Hasanno vendorpick vendor (10d to due)6495D MRM method dev - NPS 40.9
KAN-26Idea2026-07-10Moaraj Hasanno vendorpick vendor (10d to due)In-life dosing + serial plasma collection (0-24 h timecourse)
KAN-31Idea2026-07-18Moaraj Hasanno vendorpick vendor (18d to due)Accuracy + precision validation runs (within/between-run)
KAN-27Idea2026-07-18Moaraj Hasanno vendorpick vendor (18d to due)Bioanalysis of PK samples on validated 6495D method
KAN-12Idea2026-07-20Moaraj Hasanno vendorpick vendor (20d to due)Plasma protein binding + blood:plasma partitioning
KAN-32Idea2026-07-22Moaraj Hasanno vendorpick vendor (22d to due)Matrix effect, recovery, dilution integrity, carryover
KAN-35Idea2026-07-28Moaraj Hasanno vendorpick vendor (28d to due)Cross-species in-vitro scaling inputs (clearance, binding, stability)
KAN-28Idea2026-07-31Moaraj Hasanno vendorpick vendor (31d to due)Non-compartmental PK analysis + IV/SC parameter report
KAN-1Idea2026-07-31Moaraj Hasanno vendorpick vendor (31d to due)In-vivo PK: mouse single-dose IV/SC (NXN 20.16 + NPS 40.9)
KAN-13Idea2026-08-07Moaraj Hasanno vendorpick vendor (38d to due)In-vivo PK study report + data package of record (IV/SC)
KAN-33Idea2026-08-08Moaraj Hasanno vendorpick vendor (39d to due)Stability validation (stock, bench, freeze-thaw, long-term, autosampler)
KAN-36Idea2026-08-10Moaraj Hasanno vendorpick vendor (41d to due)Allometric scaling model (CL, Vss) + human PK prediction
KAN-38Idea2026-08-10Moaraj Hasanno vendorpick vendor (41d to due)PK/PD biomarker + exposure-response model build
KAN-37Idea2026-08-21Moaraj Hasanno vendorpick vendor (52d to due)Human starting dose: MABEL + NOAEL/BSA HED + safety factor
KAN-4Idea2026-08-21Moaraj Hasanno vendorpick vendor (52d to due)Allometric Scaling & Human Starting Dose
KAN-34Idea2026-08-28Moaraj Hasanno vendorpick vendor (59d to due)ICH M10 bioanalytical validation report sign-off
KAN-3Idea2026-08-28Moaraj Hasanno vendorpick vendor (59d to due)Bioanalytical Method & ICH M10 Validation (6495D)
KAN-39Idea2026-08-28Moaraj Hasanno vendorpick vendor (59d to due)Clinical dose-escalation scheme + projected exposure margins
KAN-5Idea2026-08-28Moaraj Hasanno vendorpick vendor (59d to due)PK/PD Linkage & Dose Escalation

Safety + immunogenicity

4 open 0 done
CRO progress (Drive): 📁 Tox Studies
KeyStatusDueAssigneeVendorCRO progressSummary
KAN-43Idea2026-07-21Moaraj Hasanno vendorpick vendor (21d to due)In-vitro safety pharmacology (hERG, cardiovascular liability)
KAN-44Idea2026-08-10Moaraj Hasanno vendorpick vendor (41d to due)Immunogenicity / ADA assay strategy + in-silico risk
KAN-45Idea2026-08-31Moaraj Hasanno vendorpick vendor (62d to due)GLP tox study design + DART deferral justification
KAN-7Idea2026-08-31Moaraj Hasanno vendorpick vendor (62d to due)Safety & Immunogenicity (DART defer, ADA)

GLP / CMC outsourcing

8 open 0 done
KeyStatusDueAssigneeVendorCRO progressSummary
KAN-71Idea2026-09-08Moaraj Hasanno vendorpick vendor (70d to due)GMP clinical batch manufacture (API) + batch record + CoA
KAN-69Idea2026-09-15Moaraj Hasanno vendorpick vendor (77d to due)Genotoxicity battery (Ames + in vitro micronucleus)
KAN-67Idea2026-09-15Moaraj HasanCharles River Laboratories · no contract no_contractGLP repeat-dose toxicology study (rodent) - execution + report
KAN-72Idea2026-09-22Moaraj Hasanno vendorpick vendor (84d to due)Drug product CMC: sterile injectable formulation, fill-finish, container-closure
KAN-70Idea2026-09-22Moaraj HasanCharles River Laboratories · no contract no_contractSafety pharmacology core battery (ICH S7A: CV, CNS, respiratory)
KAN-68Idea2026-09-22Moaraj Hasanno vendorpick vendor (84d to due)GLP repeat-dose toxicology study (non-rodent) - execution + report
KAN-73Idea2026-09-29Moaraj Hasanno vendorpick vendor (91d to due)ICH Q1A stability program on clinical API + DP lots
KAN-8Idea2026-09-30Moaraj Hasanno vendorpick vendor (92d to due)GLP Outsourcing & CMC (engage on clinical lead)

Regulatory (AU CTN)

3 open 0 done
CRO progress (Drive): 📁 Phase 1 trial
KeyStatusDueAssigneeVendorCRO progressSummary
KAN-75Idea2026-09-15Moaraj Hasanno vendorpick vendor (77d to due)Clinical protocol + synopsis (FIH SAD)
KAN-74In Progress2026-09-22Moaraj Hasanno vendorpick vendor (84d to due)Author Investigator's Brochure (IB)
KAN-9Idea2026-09-30Moaraj Hasanno vendorpick vendor (92d to due)AU CTN Regulatory Package & Submission